Rare diseases and orphan products : accelerating research and development / Committee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies.

Other author Field, Marilyn J. (Marilyn Jane)
Other author Boat, Thomas F.
Other author Institute of Medicine (U.S.). Committee on Accelerating Rare Diseases Research and Orphan Product Development.
Format Electronic
Publication InfoWashington, DC : National Academies Press, ©2010.
Description1 online resource (442 pages) : illustrations
Supplemental ContentClick to View
Subjects
Orphan drugs.
Drugs--Design.
Rare diseases--Treatment.
Orphan Drug Production--Evaluation Studies.
Rare Diseases--drug therapy. --Evaluation Studies.
Drug Discovery--Evaluation Studies.
Drug Evaluation--Evaluation Studies.
Health Policy--Evaluation Studies.
Policy Making--Evaluation Studies.

Contents Profile of rare diseases -- Regulatory framework for drugs for rare diseases -- Discovery research for rare diseases and orphan product development -- Development of new therapeutic drugs and biologics for rare diseases -- Coverage and reimbursement : incentives and disincentives for product development -- Medical devices : research and development for rare diseases -- Toward an integrated approach to accelerating research and product development for rare diseases -- Study activities -- Innovation and the Orphan Drug Act, 1983-2009: regulatory and clinical characteristics of approved orphan drugs -- Medicare Part D coverage and reimbursement of orphan drugs -- Glossary, abbreviations, and public laws -- Rare Diseases Clinical Research Network -- Advocacy group approaches to accelerating research and product development: illustrative examples.
Abstract "Rare diseases collectively affect millions of Americans of all ages, but developing drugs and medical devices to prevent, diagnose, and treat these conditions is challenging. The IOM recommends implementing an integrated national strategy to promote rare diseases research and product development."--Publisher's description.
Local noteLaupus-WCP
General noteTitle from resource title page (National Academies Press, viewed Mar. 9, 2011).
Bibliography noteIncludes bibliographical references.
Issued in other formAlso available in print: Rare diseases and orphan products. Washington, DC : National Academies Press, c2010. 9780309158060 0309158060
Genre/formElectronic books.
ISBN9780309158077 (pdf)
ISBN0309158079 (pdf)